January 2015
Together we can Cure Duchenne!
Research
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CureDuchenne Ventures LLC to Provide $1 Million to Capricor Therapeutics to Advance Promising Research to Treat Heart Disease Associated with Duchenne Muscular Dystrophy

CureDuchenne Ventures LLC, a company that funds research to find a cure for Duchenne muscular dystrophy that was formed by the nonprofit CureDuchenne, announced on January 12 that they are investing $1 million in Capricor Therapeutics...

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CureDuchenne Seeds Collaborative Project to Analyze the History of Duchenne Muscular Dystrophy

CureDuchenne announced on January 13 that the organization is funding Dr. Susan J. Ward, a consultant to BioPharma, in partnership with Dr. James Signorovitch, Vice President at Analysis Group Inc....

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Sarepta Therapeutics Reports Long-Term Outcomes through 168 Weeks from Phase IIb Study of Eteplirsen in Duchenne Muscular Dystrophy

Sarepta Therapeutics released the 168 week data for their exon skipping drug, eteplirsen, on January 12. During a three year period, 7-13 year old boys with Duchenne (the age range of the boys who began the 201 study)...

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Sarepta Therapeutics Announces First Patient Dosed in European Phase I/II Study of SRP-4053 in Duchenne Muscular Dystrophy Patients

Sarepta Therapeutics Inc. (NASDAQ: SRPT), a developer of RNA-based therapeutics, announced on January 14 that it has initiated dosing of SRP-4053 in its first human trial...

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Update on Phase 3 tadalafil DMD study: enrollment completed

CureDuchenne is pleased to share the following update to the Duchenne muscular dystrophy community from Lilly regarding the ongoing Phase 3 trial of tadalafil in boys with Duchenne...

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BioMarin CEO Sees Big Future For Prosensa Drug

During BioMarin’s investor day executives said that their experience in launching orphan drugs should help them get drisapersen approved on the phase II data...

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PTC Therapeutics Begins Rolling NDA Submission to the FDA for Translarna to Treat Duchenne Muscular Dystrophy

PTC Therapeutics, Inc. (NASDAQ: PTCT) announced on December 23 that it has commenced a rolling submission of a New Drug Application (NDA) to the United States Food and Drug Administration (FDA) for Translarna™ for the treatment of nonsense mutation Duchenne muscular dystrophy (nmDMD)...

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News
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CureDuchenne Launches CureDuchenne Cares, a Physical Therapy, Education and Outreach Program for the Duchenne Community

CureDuchenne launched CureDuchenne Cares, a physical therapy, education and outreach program for the Duchenne community on January 26...

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Napa in Newport Wine Auction on February 28 Features More Than 20 Napa Wineries and Benefits CureDuchenne

NEWPORT BEACH, Calif., January 29, 2015 CureDuchenne, a nonprofit that raises awareness and funds research to find a cure for Duchenne muscular dystrophy, announced today that they will host a Napa in Newport Wine Auction on February 28...

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Recent Success
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NHL Hockey Player Ryan Getzlaf Inspired by Hawken Miller Who Lives With Duchenne

NHL Hockey Player Ryan Getzlaf and 18-year-old Hawken Miller have formed a friendship. Find out more about their heartwarming story...

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Global Genes RARECast Features Debra Miller

Host Daniel Levine of Levine Media Group and creator of The Bio Report breaks new ground in this weekly online series RARECast, the new Global Genes podcast...

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CureDuchenne Founder Presented at Life Science Nation Conference

Debra Miller, founder and CEO of CureDuchenne presented at the Life Science Nation Redefining Early Stage Investments conference on January 13 in San Francisco...

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Duchenne Therapy Network
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Newest Video

Duchenne Therapy Network and CureDuchenne are pleased to share the newest video. Thank you to Scott Brown for sharing your thoughts and experiences with yoga...

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Duchenne Research and Physical Therapy Update

CureDuchenne and Duchenne Therapy Network will host a Duchenne research and physical therapy update on March 14 in Toledo, Ohio...

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Upcoming Events
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Napa in Newport Wine Auction, February 28, 2015, Newport Beach, Calif.

Reserve the date for the Champions to CureDuchenne Napa in Newport Wine Auction on February 28, 2015. Once again this event will be held at the Balboa Bay Club in Newport Beach, Calif...

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Duchenne Research and Physical Therapy Update, March 14, Toledo, Ohio

CureDuchenne and Duchenne Therapy Network will host a Duchenne research and physical therapy update on March 14 in Toledo, Ohio...

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Champions to CureDuchenne, April 11, 2015, Austin, Texas

Save the date for the Champions to CureDuchenne Austin on April 11 at the University of Texas Golf Club. Vince Young hosts the event. This Texas-sized tailgate party will feature music, gourmet food and silent and live auction...

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Blingo to CureDuchenne, April 11, 2015, Philadelphia

Blingo is back. Save the date for Blingo to CureDuchenne on April 11 at the Rittenhouse Hotel in Philadelphia...

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