February 2016
Together we can Cure Duchenne!
Research
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Capricor Therapeutics Announces the First Patient with Duchenne Muscular Dystrophy-Related Cardiomyopathy Treated with CAP-1002 in the HOPE-Duchenne Phase I/II Clinical Trial

Capricor Therapeutics, Inc. (NASDAQ: CAPR), a biotechnology company focused on the discovery, development and commercialization of first-in-class therapeutics, today announced continuing enrollment of, and the treatment of the first patient with Duchenne Muscular Dystrophy (DMD)-related cardiomyopathy with CAP-1002 in the HOPE-Duchenne Phase I/II clinical trial (Halt cardiomyOPathy progrEssion in Duchenne)...

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Sarepta Therapeutics Receives Notification of PDUFA Extension for Eteplirsen

Sarepta Therapeutics, Inc. (NASDAQ:SRPT), a developer of innovative RNA-targeted therapeutics,  announced on February 8 that the U.S. Food and Drug Administration (FDA) will require additional time to complete its review of the New Drug Application (NDA) for eteplirsen, for the treatment of Duchenne muscular dystrophy (DMD) amenable to exon 51 skipping...

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PTC Receives Refuse to File Letter from FDA for Translarna™ (ataluren)

PTC Therapeutics, Inc. (NASDAQ: PTCT) announced on February 23 that it received yesterday evening a Refuse to File letter from the United States Food and Drug Administration (FDA) regarding PTC's New Drug Application (NDA) for Translarna™ (ataluren), an oral, first-in-class, protein restoration therapy for the treatment of nonsense mutation Duchenne muscular dystrophy (nmDMD)...

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Duchenne Research Highlights from MDA Conference

Update on Phase 3 Tadalafil Trial

We are sharing the following information from Lilly on their Phase 3 Tadalafil trial...

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CureDuchenne Cares
Abilities Expo Video Blog

Everything is Bigger in Texas

The CureDuchenne Cares team was greeted with such enthusiasm by the Duchenne community in and around the Austin area while bringing their free, educational Family and Caregiver workshop on January 30th...

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Abilities Expo Video Blog

CureDuchenne Cares Brings a Robust Program to Riverside, CA

The CureDuchenne Cares program was created to answer the call of parents and family members who needed advice and best practices for managing various facets of Duchenne muscular dystrophy...

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News
Vince Young Hosts Champions to CureDuchenne Event to Find a Cure for Duchenne Muscular Dystrophy

Napa In Newport Live Auction

We look forward to seeing you at Napa In Newport on February 27! We have some amazing auction items. This is your opportunity to bid on one-of-kind experiences while helping to save the lives of those with Duchenne....

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Vince Young Hosts Champions to CureDuchenne Event to Find a Cure for Duchenne Muscular Dystrophy

Comprehensive Neuromuscular Center Earns Top Recognition

Congratulations to Dr. Brenda Wong and her team at the Comprehensive Neuromuscular Care Center at Cincinnati Children's Hospital Medical Center for earning top recognition by the National Committee for Quality Assurance as Level 3 Patient-Centered Specialty Practice...

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Recent Success
Vince Young Hosts Champions to CureDuchenne Event to Find a Cure for Duchenne Muscular Dystrophy

Walk to CureDuchenne Raises More than $20,000

The inaugural The Walk to CureDuchenne, in partnership with The Paramount Break-A-Leg 5K, brought together family and friends in Austin, TX on February 14, 2016. More than 40 walkers wore CureDuchenne t-shirts and capes in a celebration of life and progress of CureDuchenne and the families they serve...

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Vince Young Hosts Champions to CureDuchenne Event to Find a Cure for Duchenne Muscular Dystrophy

Boys with Duchenne Inspire 100 Mile Race

A friend of Tim Revell, a father of two boys with Duchenne, who he has run with and known for the past two years completed an incredible feat over the weekend. She became the first person to wear a CureDuchenne shirt while completing a 100 Mile Race...

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Upcoming Events
CureDuchenne Venture Philanthropy Model Featured in Forbes Insight Report

Napa in Newport, February 27, St. Regis Hotel, Dana Point, CA

Napa in Newport is Southern California's premier wine event. Napa in Newport brings together 40 of Napa's best wineries and world class chef for a truly unforgettable experience. It will be held on February 27, 2016 at the St. Regis Hotel in Dana Point, Calif...

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CureDuchenne Venture Philanthropy Model Featured in Forbes Insight Report

CureDuchenne Cares Workshop for Families, March 12, Fort Lauderdale, FL

Please join CureDuchenne Cares for a free, informative class on Duchenne muscular dystrophy on March 12 in Fort Lauderdale, FL for family members and caregivers at the Embassy Suites Fort Lauderdale, 110 SE 17th Street, Fort Lauderdale, FL 33316.

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CureDuchenne Venture Philanthropy Model Featured in Forbes Insight Report

Champions to CureDuchenne Austin, April 9, Austin, TX

Save the date for the Champions to CureDuchenne Austin event on April 9, 2016 in Austin, TX. This annual event will benefit CureDuchenne and is presented by Johnny Carino’s...

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CureDuchenne Venture Philanthropy Model Featured in Forbes Insight Report

CureDuchenne Cares Workshop for Families, Houston, April 9

Please join CureDuchenne Cares for a free, informative class on Duchenne muscular dystrophy on April 9 in Houston, TX for family members and caregivers at the T.E.A.M Approach: 13150 FM 529, Suite 114, Houston, TX 77041...

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CureDuchenne Venture Philanthropy Model Featured in Forbes Insight Report

CureDuchenne Cares Workshop for Families, April 23, Kansas City, MO

Please join CureDuchenne Cares for a free, informative class on Duchenne muscular dystrophy on April 23 in Kansas City, MO for family members and caregivers at the Don Chrisholm Learning Center, 610 E 22nd St., Kansas City, MO from 9 a.m. 2 p.m...

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CureDuchenne Venture Philanthropy Model Featured in Forbes Insight Report

Blingo to CureDuchenne, April 30, Philadelphia, PA

Join us for Blingo to CureDuchenne on April 30 at 7 p.m. at The Logan in Philadelphia, Center City’s newest hotel.  Blingo is a night of celebrity bingo, bling and celebration where Philadelphians come together to help make a huge difference in the lives of those with Duchenne muscular dystrophy...

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